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CLINICAL TRIALS IN RETT SYNDROME
Expected Outcomes of the Workshop Publication of Proceedings of the Workshop
The Editor-in-Chief of the Journal of Child Neurology, Dr. R. Brumback has committed to publishing the proceedings of the conference.

Summary and Recommendations
The P.I and Co-P.I’s, and session chairs will prepare a report summarizing the key points raised in each of the five workshop sessions and during the two roundtables. In addition to a brief description of the state of current knowledge on clinical trials in RTT and related fields, the report will focus on those areas identified as needing further research. The report will be communicated to appropriate staff at the sponsoring NIH institutes (i.e., NICHD, NINDS), other pertinent government agencies (e.g., FDA), and private agencies that fund RTT and related research.

Stimulation and Encouragement of Young Scientists
By encouraging participation of trainees and junior faculty, the organizers hope that younger RTT researchers might continue to pursue careers in areas relevant to the workshop’s agenda. This will be facilitated in part by the junior research travel awards program.

New Projects and Collaborative Initiatives
Considering that the workshop has been planned and organized by members of the International Consortium for Rett Syndrome Research, it is not only expected that this workshop will stimulate the involvement in clinical trials-related projects by established researchers in RTT but also that it will facilitate the development of new collaborations. Of particular relevance to RTT, a relatively rare disorder, is the possibility of establishing multi-center studies which will allow the inclusion of larger samples and/or a focus on a particular RTT genetic background or stage.

Future Meetings
It is anticipated that this workshop will generate significant enthusiasm among the participants to warrant holding additional conferences in the future. We project that a biennial meeting would be beneficial in order to assess progress, to propose new research directions, and to continue foster research collaborations.